What it is
Sickle cell anemias are chronic hemolytic diseases that may induce three types of acute accidents: severe anemia, severe bacterial infections, and ischemic vasoocclusive accidents (VOA) caused by sickle-shaped red blood cells obstructing small blood vessels and capillaries. Many diverse complications can occur.
Sickle cell disease (SCD) is a group of inherited red blood cell disorders. If you have SCD, there is a problem with your hemoglobin. Hemoglobin is a protein in red blood cells that carries oxygen throughout the body. With SCD, the hemoglobin forms into stiff rods within the red blood cells. This changes the shape of the red blood cells. The cells are supposed to be disc-shaped, but instead they are crescent, or sickle, shaped.The sickle-shaped cells are not flexible and cannot change shape easily. Many of them burst apart as they move through your blood vessels. The sickle cells usually only last 10 to 20 days, instead of the normal 90 to 120 days. Read more at MedlinePlus.
Source: Monarch Initiative, MONDO:0011382 and MedlinePlus, fetched 2026-11-10.
Causes
Gene associations arrive in a later milestone.
MedlinePlus has a plain-language page on causes and risk factors: Sickle Cell Disease.
Source: MedlinePlus, fetched 2026-11-10.
Approved treatments
7 drugs whose FDA (United States) label names this disease under indications. Approval elsewhere differs.
- Crizanlizumab (Adakveo)
d to reduce the frequency of vaso-occlusive crises (VOCs) in adults and pediatric patients aged 16 years and older with sickle cell disease. ADAKVEO is a selectin blocker indicated to reduce the frequency of vasoocclusive crises in adults and pediatric patients aged 16 years and older with sickle cell disease.
- Deferiprone (Ferriprox)
ent of transfusional iron overload in adult and pediatric patients 8 years of age and older with thalassemia syndromes, sickle cell disease or other anemias. Limitation s of Use • Safety and effectiveness have not been established for the treatment of transfusional iron overload in patients with myelodysplastic syndrom
- Exagamglogene Autotemcel (Casgevy)
1. INDICATIONS AND USAGE CASGEVY is indicated for the treatment of patients aged 2 years and older with: sickle cell disease (SCD) with recurrent vaso-occlusive crises transfusion-dependent β - thalassemia (TDT) CASGEVY is an autologous genome edited hematopoietic stem cell-based gene therapy indicated f
- Glutamine (Endari)
Endari is indicated to reduce the acute complications of sickle cell disease in adult and pediatric patients 5 years of age and older. ENDARI is an amino acid indicated to reduce the acute complications of sickle cell disease in adult and pediatric patients
- L-Glutamine
L-glutamine oral powder is indicated to reduce the acute complications of sickle cell disease in adult and pediatric patients 5 years of age and older. L-glutamine oral powder is an amino acid indicated to reduce the acute complications of sickle cell disease in adult and p
- Lovotibeglogene Autotemcel (Lyfgenia)
LYFGENIA is indicated for the treatment of patients 12 years of age or older with sickle cell disease and a history of vaso-occlusive events. LYFGENIA is an autologous hematopoietic stem cell-based gene therapy indicated for the treatment of patients 12 years of age or older with s
- Voxelotor (Oxbryta)
OXBRYTA is indicated for the treatment of sickle cell disease (SCD) in adults and pediatric patients 4 years of age and older. This indication is approved under accelerated approval based on increase in hemoglobin (Hb) [see Clinical Studies (
Source: openFDA drug labels, fetched 2026-11-10.
Latest research
The newest randomized trials, meta-analyses and systematic reviews with this disease in the title. 632 in total.
- A qualitative evidence synthesis on perinatal screening for sickle cell disease in high-burden countries
- Efficacy and safety of mitapivat in patients with sickle cell disease (RISE UP): a phase 3, double-blind, global, randomised, placebo-controlled trial
- Local ancestry-aware genome-wide meta-analysis uncovers novel genetic loci for sickle cell disease nephropathy
- Red blood cell transfusion to treat or prevent complications in sickle cell disease: an overview of Cochrane reviews
- Global burden of moyamoya syndrome in pediatric sickle cell disease and implications for the neurosurgical workforce: a systematic review
- A Phase IIa, Double Blind, Randomized, Placebo Controlled, Parallel, Multicentre, Proof-of-Concept Study to Evaluate the Efficacy and Safety of Desidustat Oral Tablet for Treatment of Sickle Cell Disease
- Benefit-risk of voxelotor, crizanlizumab, and l-glutamine in sickle cell disease: A systematic review
- Prevalence and risk factors of red blood cell alloimmunization among sickle cell disease patients in resource-limited countries: A systematic review and meta-analysis
- Adenotonsillectomy in children with sickle cell disease: a systematic review
- Secretory Phospholipase A<sub>2</sub> in Patients With Sickle Cell Disease Hospitalized for Vaso-Occlusive Pain Episodes
- Methodological Quality and Content Analysis of Clinical Practice Guidelines for Fever Management in Children With Sickle Cell Disease
- From Stigma to Suffering: Stigma, Health-Related Quality of Life, and Healthcare Access in Sickle Cell Disease-A Global Systematic Review
- AI-assisted decision support for sickle cell disease severity stratification using routine blood tests: a systematic review and meta-analysis
- Cochlear Implantation in Sickle Cell Disease: A Systematic Review of Feasibility and Outcomes
- Design, rationale, and baseline patient characteristics for the Sickle Cell Disease and CardiovAscular Risk-Red cell Exchange (SCD-CARRE) trial
- Nanotechnology-Based Detection of Sickle Cell Disease and Thalassemia: A Systematic Review
- Efficacy, Safety, and Treatment-Delivery Feasibility of Autologous Gene Therapy for Sickle Cell Disease: A Systematic Review With Descriptive Synthesis of Clinical Trials
- Vitamin B12 Deficiency in Sickle Cell Disease: Method-Driven Estimates and Systematic Diagnostic Misclassification
- Orbital involvement in sickle cell disease: A systematic review
- Effect of fully immersive virtual reality on daily pain, functional mobility, and health-related quality of life in pediatric sickle cell disease: a single-blinded randomized clinical trial
Source: Europe PMC, fetched 2026-11-10.
Trials recruiting now
211 studies on ClinicalTrials.gov are recruiting (165) or about to (46). Most advanced first. Phase 3 is the last step before approval; Phase 1 is the first time in people.
Phase 4 8 Phase 3 16 Phase 2/3 2 Phase 2 27 Phase 1/2 19 Phase 1 13 Early phase 1 4 No phase given 61 Observational 61
Loading all 211 trials for filtering…
Phase 4, after approval 8
- Integrating Point of Care Testing (POCT) For Newborn Screening and Early Care for Sickle Cell Disease in Yopougon, Côte d'Ivoire
- Clinical and Biomarker Effects of Depot Medroxyprogesterone Acetate in Females With Sickle Cell Disease
- Effectiveness of Nontraditional Hydroxyurea Algorithms: Novel and Clinical Evaluations (ENHANCE)
- Stroke Prevention in Nigeria 2 Trial
- Rollover Study for Patients With Sickle Cell Disease Who Have Completed a Prior Novartis-Sponsored Crizanlizumab Study
- Adaptive Platform Trial for Pain Management in Sickle Cell Vaso-Occlusive Crisis
- Low Dose Bolus Ketamine For Use In Sickle Cell Pain Crisis
- Ketorolac for Acute Vaso-Occlusive Crisis in Pediatric Sickle Cell Disease
Phase 3 16
- A Study to Investigate the Effect of Mitapivat on Transfusion Burden in Subjects With Sickle Cell Disease (SCD)
- Lidocaine for Opioid Sparing in Vaso-occlusive Crisis of Sickle Cell Disease
- Study of a Single Dose of a 21-valent Pneumococcal Conjugate Vaccine in Children and Adolescents With Sickle Cell Disease
- Efficacy and Safety of Tocilizumab for Acute Chest Syndrome Treatment in Patients With Sickle Cell Disease
- The Efficacy and Safety of Rilzabrutinib in Participants Aged 10 to 65 Years With Sickle-cell Disease
- A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease
- A Research Study Looking at Long-term Treatment With Etavopivat in People With Sickle Cell Disease or Thalassaemia
- A Study to Investigate the Efficacy and Safety of Crizanlizumab (5 mg/kg) Compared With Placebo in Adolescent and Adult Sickle Cell Disease Patients Who Experience Frequent Vaso-Occlusive Crises (SPARKLE)
- Promoting Utilization and Safety of Hydroxyurea Using Precision in Africa
- RElated Haplo-DonoR Haematopoietic stEm Cell Transplantation for Adults With Severe Sickle Cell Disease
- Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
- Evaluation of the Efficacy of Iloprost in the Management of Vaso-occlusive Crises in Adult Patients With Sickle Cell Disease
- Analgesic Effect of Parecoxib Versus Morphine in SCD Patients Presenting to the Emergency Department
- Optimal Timing of Ketamine Initiation for SCD Pain
- A Study of Intravenous L-Citrulline in Patients Aged 6-21 Years Old With Sickle Cell Disease Presenting to Emergency Departments in Acute Vaso-Occlusive Crisis
- Intranasal Sufentanil for Analgesia of Severe Sickle Cell Vaso-occlusive Pain Crisis in the Pediatric
Phase 2/3 2
Phase 2 27
- Efficacy and Safety of SIL-8301 for Control of Hemolysis in a Uniform Sickle Cell Disease Endotype
- Sub-dissociative Dose Ketamine in Treatment of Vaso-occlusive Pain Event in Children and Young Adults
- Haploidentical Donor Hematopoietic Cell Transplant for Sickle Cell Disease
- Targeting the Pathophysiology of Sickle Cell-Related Kidney Disease Using the SGLT2 Inhibitors, Empagliflozin
- Alendronate for Osteonecrosis in Adults With Sickle Cell Disease
- Zinc Supplementation in Sickle Cell Disease: A Precursor to the Think Zinc for Bones Trial
- Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- Early Screening and Treatment of Heart Complication in Sickle Cell Disease
- Safety, Efficacy, and Pharmacokinetics of CSL889 in Adults and Adolescents With Sickle Cell Disease During Vaso-Occlusive Crisis
- Cannabinoids for the Reduction of Inflammation and Sickle Cell Related Pain
- Pharmacokinetics, Efficacy and Safety of Twice Daily Dosing Regimen of Hydroxycarbamide Dispersible Tablets in Children With Sickle Cell Disease
- Intravenous L-Citrulline for Vaso-occlusive Pain Episode in Sickle Cell Disease
- Allo HSCT for High Risk Hemoglobinopathies
- Sickle Cell Disease Transplant Using a Nonmyeloablative Approach for Patients With Anti-donor Red Cell Antibody
- Relationship Between Abnormal Myocardial Perfusion and Diastolic Dysfunction in Sickle Cell Disease Using PET
- A Phase 2 Open-label Study to Evaluate the Activity of Etavopivat on Transcranial Doppler Velocities in Pediatric Patients With Sickle Cell Disease Who Are at Increased Risk for Primary Stroke
- Tocilizumab for Acute Chest Syndrome
- A Study of Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)
- A Study to Evaluate the Pharmacokinetics and Safety of Etavopivat in Pediatric Patients With Sickle Cell Disease
- Cognitive Remediation Intervention to Prepare for Transition of Care
- A Trial to Assess Haploidentical T-depleted Stem Cell Transplantation in Patients With SCD
- AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion
- Minimizing Toxicity in HLA-identical Sibling Donor Transplantation for Children With Sickle Cell Disease
- Nonmyeloablative Stem Cell Transplant in Children With Sickle Cell Disease and a Major ABO-Incompatible Matched Sibling Donor
- Myeloablative Conditioning, Prophylactic Defibrotide and Haplo AlloSCT for Patients With Sickle Cell Disease
- Study of HLA-Haploidentical Stem Cell Transplantation to Treat Clinically Aggressive Sickle Cell Disease
- Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
Phase 1/2 19
- Partial Stem Cell Transplant for Sickle Cell Disease From Matched Donors
- Ruxolitinib-Enhanced Haplo HCT for Children and Young Adults With Sickle Cell Disease
- Optimizing Hydroxyurea Therapy in Children With Sickle Cell Anemia In Malaria Endemic Areas: The NOHARM Maximum Tolerated Dose (MTD) Study
- Efficacy Safety Study of Gene Therapy for Sickle Cell DiseaseSCD Using Autologous CD34+ Cells Transduced ex Vivo, Carrying a Corrected Globin Gene and a Silencing RNA.
- Transplantation of Clustered Regularly Interspaced Short Palindromic Repeats Modified Hematopoietic Progenitor Stem Cells (CRISPR_SCD001) in Patients With Severe Sickle Cell Disease
- Cannabidiol in Sickle Cell Disease
- Acceptance and Commitment Therapy for Adolescents and Young Adults With Sickle Cell Disease
- A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease
- Investigation Into the Use of BAH243 Lentiviral Vector for Gene Therapy in Treating Sickle Cell Disease
- A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease
- Gene Correction in Autologous CD34+ Hematopoietic Stem Cells (HbS to HbA) to Treat Severe Sickle Cell Disease
- RH Genotype Matched RBC Transfusions
- Repeat Peripheral Blood Stem Cell Transplantation for Patients With Sickle Cell Disease and Falling Donor Myeloid Chimerism Levels
- T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias
- Reduced Intensity Conditioning and Familial HLA-Mismatched BMT for Non-Malignant Disorders
- Arginine Therapy for the Treatment of Pain in Children With Sickle Cell Disease
- Feasibility and Acceptability of Amani
- STEM CELL MOBILIZATION WITH HIGH-DOSE PLERIXAFOR IN PATIENTS WITH SICKLE CELL DISEASE
- Crizanlizumab Improves Tissue Oxygen Supply Demand Matching in Patients With Sickle Cell Anemia
Phase 1 13
- Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Sickle Cell Disease
- Escalating Doses of VAS-101 in Subjects With Stable Sickle Cell Disease
- A Phase 1b, Open-Label Study of DISC-3405 in Participants With Sickle Cell Disease (SCD)
- Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
- Methylphenidate to Address Attention and Executive Deficits Among Children With Sickle Cell Disease
- 131I-apamistamab-based Conditioning for Hematopoietic Stem Cell Transplant (HSCT) in Advanced Sickle Cell Disease (SCD)
- Gene Editing For Sickle Cell Disease
- Study to Evaluate the Safety and Tolerability of Escalating Doses of Fostamatinib in Subjects With Stable Sickle Cell Disease
- SCD Stem Cell Mobilization and Apheresis Using Motixafortide
- A Study of Nicotinamide With Oral Tetrahydrouridine and Decitabine to Treat High Risk Sickle Cell Disease
- Study of Panobinostat (LBH589) in Patients With Sickle Cell Disease
- Buprenorphine for the Management of Pain in Children With Sickle Cell Disease
- Minocycline In Neurocognitive Outcomes - Sickle Cell Disease
Early phase 1 4
No phase given 61
- Virtual Reality for SCD VOC
- Assessing Molecular Mechanisms and Effects of Music Therapy in Youth With Sickle Cell Disease Using Single-cell RNA-sequencing
- Early Life Exposures Among Children With Sickle Cell Disease
- Integrative Medicine in Pain Management in Sickle Cell Disease, 2.0
- SickleFit Exercise and Nutrition Study
- Evaluation of an Information Management and Communication System for Population-wide Point-of-Care Infant Sickle Cell Disease Screening
- Morphine Clearance and Glomerular Filtration in Sickle Cell Patients in Crisis in Intensive Care
- Writing Relaxing Beats in Adolescents Who Have Sickle Cell Disease
- Multi Disciplinary Sickle Cell Disease Obstetrics Care Program in Ghana
- Stress Management and Mindfulness Intervention for Patients With Sickle Cell Disease
- A Smart Phone Application to Improve Adoption of the 2024 Kidney Disease Improving Global Outcomes (KDIGO) Chronic Kidney Disease (CKD) Guidelines
- Delivering Patient-Facing Evidence-Based Guidelines Through mHealth to Adults With Sickle Cell Disease
- Promoting Resilience Among Adolescents and Young Adults With Sickle Cell Disease
- Efficacy of Liberal Versus Restricted IV Fluid Approach in the Management of Sickle Cell Vaso-Occlusive Crisis
- Cerebrovascular Reactivity Measurements With High-Density Diffuse Optical Tomography
- Trans-auricular Nerve Stimulation as an Innovative Approach to the Treatment of Pain in Pediatric Patients Suffering From Sickle Cell Disease
- Exploratory Study on Global Reflexology in Sickle Cell Disease
- MULTIsite Feasibility of MUSIc Therapy to Address Quality Of Life in Sickle Cell Disease
- School Readiness Intervention for Preschool Children With Sickle Cell Disease
- Peer Support for Adolescents and Emerging Adults With Sickle Cell Pain
- Pilot Study "AHSP as a Biomarker of Sickle Cell Disease in a Population of Adults and Children"
- Advancing Feasibility and Acceptability of Digital Cognitive Rehabilitation in Sickle Cell Disease
- A Socio-ecological Approach for Improving Self-management in Adolescents With SCD
- Adapting the FACETS Program to Sickle Cell Disease
- Integrative Training Program for Pediatric Sickle Cell Pain
- Pulmonary Functions in Sickle Cell Disease: Response to Acu-TENS
- Let's Get REAL: Family Health Communication Tool in Pediatric Stem Cell Transplant and Cellular Therapy
- Empowering Adolescents and Young Adults With Sickle Cell Disease as Partners in Treatment Decision Making (EMPOWER-AYA)
- Autologous Testicular Tissue Transplantation
- Virtual Reality Devices as an Adjunct to Usual Care for Patients With Sickle Cell Disease Experiencing Vaso-Occlusive Crises
- Effect of EMDR for Reduction of Pain Interference in Children With Sickle Cell Disease
- Virtual Reality As Adjunct Therapy for Vaso-Occlusive Pain
- Long-term Endurance Training in Sickle Cell Disease Patients: Impact on Clinical Profile, Physical Fitness, and Quality of Life.
- Predictors of Pain in Sickle Cell Disease
- mAnaging siCkle CELl disEase Through incReased AdopTion of hydroxyurEa in Nigeria
- SMYLS Multi-site Trial
- Fetal Cell Receptors Repertoire
- Pressure Pain Tolerance in Relation to Balance and Strength in Children
- Feasibility and Efficacy of Attentional-Control Training in Sickle Cell Disease
- Cutaneous Hydration Assessment in SCD
Showing the 40 most recent of 61. See every one on ClinicalTrials.gov.
Observational, no treatment given 61
- Functional Ovarian Reserve in Sickle Cell Disease
- Hydroxyurea Optimisation in Sickle Cell Disease
- A Long-term Follow-up Study in Patients Who Received BEAM-101
- Study to Understand the Genetic Risk of Developing an Immune Response After Blood Transfusions Among Individuals With Sickle Cell Disease
- PASS of Xromi Comparing Safety and Effectiveness in Children Under 2 Years With Sickle Cell Disease [PRECISE PASS]
- Verifying Antibodies After Live Immunization Delivery (VALID): A Study of Measles Vaccine Immunogenicity in Children With Sickle Cell Disease
- Phenotypic and Transcriptomic Description of Megakaryocytes in Sickle Cell Patient
- Impact of Regional Anesthesia on Inflammatory Mechanisms During Vaso-occlusive Crisis in Sickle Cell Patients
- Study of Vitamin B12 Metabolism in Children With Sickle Cell Disease Exposed to MEOPA
- ATHNdataset Registry
- Development of Non-Invasive Prenatal Diagnosis for Single Gene Disorders
- Peripheral Arterial Tonometry and Neurocognition in Sickle Cell Disease
- Sickle Cell Kidney Biorepository
- HPC Offered for PRESERVE Expansion
- Molecular and Cellular Basis of Severe Forms of Dengue in Sickle Cell Patients
- Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease
- Hemoglobin Disorders in Egypt: Sickle Cell Disease Ain Shams University Institutional Registry
- Serial Assessment of Fertility Experiences
- Recruitment and Engagement in Care to Impact Practice Enhancement (RECIPE) for Sickle Cell Disease
- Gene Therapy Communication: Use of a Needs Assessment to Drive Decision-AIDS for Gene Therapy for Rare Diseases (GENETX)
- Achieving Understanding of the Natural History of Sickle Cell Trait (AUNT)
- Study of the Role of Genetic Modifiers in Hemoglobinopathies
- Bone Loss, Physical Function and Frailty in Older Women With Sickle Cell Trait Sickle Cell Trait
- Domestication and Implementation of the PEN-Plus Clinical Model in the Zambian Health System
- European Rare Blood Disorders Platform (ENROL)
- Dietary Intake and Dietary Behaviors in Adults With Sickle Cell Disease
- Observational Study to Deeply Phenotype Major Organs in Sickle Cell Disease After Curative Therapies
- RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs)
- Sickle Cell Disease and the Genomic and Gene Therapy Needs of Stakeholders
- Integrative Diagnosis for SCD and Other RADs
- ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
- Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- Hydroxyurea Exposure Limiting Pregnancy and Follow-Up Lactation
- A Pilot Study on Neuroimaging in SCD: Part of The Boston Consortium to Cure Sickle Cell Disease
- Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants
- Genotype -Phenotype Correlation of PKLR Variants With Pyruvate Kinase, 2,3-Diphosphglycerate and Adenosine Triphosphate Activities in Red Blood Cells of People With Sickle Cell Disease
- Sickle-cell Disease Registry of the GPOH
- Physiology and Pathologies Linked to Human Splenic Function : Direct and Ex-vivo Perfusion Explorations
- Investigation of the Genetics of Hematologic Diseases
- Sickle Cell Disease Biofluid Chip Technology (SCD BioChip)
Showing the 40 most recent of 61. See every one on ClinicalTrials.gov.
Source: ClinicalTrials.gov, fetched 2026-11-10.
Where to go
Institutions running these trials, by country. The country picker in the trials section narrows this list too.
🇺🇸United States596
Atlanta
- Children's Healthcare of Atlanta 5
- Emory University 3
- Children's Healthcare Atlanta 2
- Emory University School of Medicine 2
- Site # 8400006 1
- Site # 8400002 1
- Children's Center for Advanced Pediatrics 1
- Arthur M. Blank Hospital- Children's Healthcare of Atlanta 1
- Arthur M. Blank Hospital-Children's Healthcare of Atlanta 1
- Winship Cancer Institute of Emory University 1
- Children's Healthcare fo Atlanta at Hughes Spalding 1
- Children's Healthcare of Atlanta at Arthur M. Blank Hospital 1
- Children's Hospital of Atlanta: Eagelston 1
- Arthur M. Blank Hospital | Children's Healthcare of Atlanta 1
- Children's Healthcare of Atlanta - Aflac Cancer and Blood Disorders Center- Egleston 1
- Children's Healthcare of Atlanta (MRD-HCT) 1
- Comprehensive Bleeding Disorders Center at Emory University and Children's Healthcare of Atlanta 1
- Emory/Children's Health Care of Atlanta 1
Memphis
- St. Jude Children's Research Hospital 14
- University of Tennessee Health Science Center- Site Number : 8400045 1
- University of Tennessee Health Science Center 1
- St. Jude Children's Res Hosp 1
- Methodist University Hospital 1
- St Jude Children's Research Hospital 1
- Methodist Comprehensive Sickle Cell Center 1
- St Jude Children Hospital (NT-DMT) 1
- St. Jude Children's Research Hospital (MRD-HCT) 1
- University of Tennessee at Memphis 1
- Regional One Health, Diggs-Kraus Sickle Cell Center 1
- Methodist Adult Comprehensive Sickle Cell Center 1
Houston
- UT Health University of Texas 2
- Baylor College of Medicine 2
- University of Texas Health Science Center at Houston 1
- Site # 8400004 1
- Baylor College of Medicine- Site Number : 8400055 1
- UT Physicians - Memorial Hermann- Site Number : 8400052 1
- Texas Children's Hospital_Houston 1
- Texas Childrens Cancer and Hematology Center 1
- U of TX Health Science Ct 1
- McGovern Medical School at UTHealth 1
- Memorial Hermann Hospital, Texas Medical Center - Clinical Research Unit (CRU) 1
- The University of Texas Health Science Center at Houston 1
- UT Physicians Comprehensive Sickle Cell Clinic 1
- UT Physicians Comprehensive Adult Sickle Cell Center 1
- UT Health Science Center 1
- Texas Children's Hopsital (NT-DMT) 1
- Texas Children's Hospital (MRD-HCT) 1
- University of Texas at Houston 1
- UT Health Houston 1
- Gulf States Hemophilia and Thrombophilia Center 1
- Texas Children's Hemophilia & Thrombosis Center/Baylor College of Medicine 1
- UT MD Anderson Cancer Center 1
Chicago
- University of Illinois at Chicago 4
- Univer Of Illinois at Chicago 2
- University of Illinois Hospital and Health Sciences System 2
- University of Illinois-Chicago - College of Medicine- Site Number : 8400054 1
- Childrens Hospital of Chicago 1
- Uni of Illinois Hospital and HSC 1
- University of Illinois at Chicago Clinical Research Center 1
- University of Illinois Hospital and Health Sciences System - Investigational Drug Services (IDS) 1
- University of Illinois Chicago, Sickle Cell Center 1
- University of Chicago 1
- Ann & Robert H. Lurie Children's Hospital of Chicago 1
- Local Institution - 0034 1
- University of Illinois at Chicago College of Medicine 1
- Ann and Robert H. Lurie Children's Hospital of Chicago 1
- Comer Children's Hospital (MRD-HCT) 1
- University of Illinois 1
- Rush University Medical Center 1
Greenville
- East Carolina University 5
- East Carolina Univ-Greenville 2
- Prisma Health- Site Number : 8400051 1
- East Carolina University_Greenville 1
- East Carolina (University of North Carolina) 1
- ECU Physicians, Brody Outpatient Clinic 1
- Prisma Health - Upstate 1
- Prisma Health Greenville Memorial Hospital 1
- Prisma Health Outpatient Radiology - Greenville 1
- Prisma Health Patewood Hospital 1
- Local Institution - 0033 1
- Local Institution - 0027 1
- Brody School of Medicine at East Carolina University 1
- Prisma Health Lifespan Comprehensive SCD Program 1
- East Carolina University Health Medical Center 1
- East Carolina University Hemophilia Treatment Center 1
Philadelphia
- Children's Hospital of Philadelphia 7
- University of Pennsylvania 2
- Childrens Hospital of Philadelphia 1
- Children's Hosptl Philadelphia 1
- St Christopher Hosp for Child 1
- Thomas Jefferson University Me 1
- Thomas Jefferson University Hospital 1
- Childrens Hospital Of Philadelphia 1
- Local Institution - 0029 1
- Thomas Jefferson University - Medicine/GI and Hepatology 1
- Children's Hospital of Philadelphia (MRD-HCT) 1
- Penn Comprehensive Hemophilia and Thrombophilia Program/Hospital of the University of Pennsylvania 1
- St. Christopher's Hospital for Children 1
New York
- Columbia University Irving Medical Center 3
- Icahn School of Medicine at Mount Sinai 2
- Mount Sinai Hospital 2
- Columbia University Medical Center_New York_0 1
- Weill Cornell Med Coll-NYPH 1
- New York Presbyterian Hospital - Morgan Stanley Children's Hospital 1
- Columbia University Medical Center 1
- Mount Sinai Medical Center 1
- Columbia University 1
- Icahn School Of Med At Mount Sinai 1
- Memorial Sloan Kettering 1
- Weil Cornell Medical College 1
- Columbia Presbytarian (NT-DMT) 1
- Weill Cornell Medical College - New York Presbyterian Hospital 1
Boston
- Boston Children's Hospital 8
- Boston Medical Center 4
- Boston Childrens Hospital 1
- Local Institution - 0024 1
- Massachusetts General Hospital 1
- Boston Children's Hospital (MRD-HCT) 1
- Boston Children's Hospital (NT-DMT) 1
- Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center 1
Birmingham
- University of Alabama at Birmingham 6
- University Of Alabama 2
- University of Alabama at Birmingham- Site Number : 8400003 1
- Uni of Alabama at Birmingham 1
- Univ of Alabama Birmingham 1
- University of Alabama Birmingham 1
- University of Alabama, Birmingham 1
- Children's of Alabama (MRD-HCT) 1
- Children's of Alabama (NT-DMT) 1
- University of Alabama, Birmingham (UAB) 1
- University of Alabama 1
Washington D.C.
- Children's National Hospital 5
- Childrens National Hospital 2
- MedStar Georgetown University Hospital- Site Number : 8400036 1
- Childrens National Medical Ctr 1
- MedStar Hlth Res Institute 1
- Children's National Medical Center 1
- Medstar Washington Hospital Center 1
- Children's National Health System 1
- Children's National Hospital (MRD-HCT) 1
- Georgetown University 1
- Children's National Hemophilia Center 1
- Childrens National Health Center 1
Bethesda
- National Institutes of Health Clinical Center 12
- Center for Cancer and Blood Disorders 1
- National Heart, Blood and Lung Institute-Cellular and Molecular Therapy Branch 1
- Suburban Hospital 1
St Louis
- Washington University-St.Louis 2
- Washington University School of Medicine 2
- St. Louis Children's Hospital 1
- Local Institution - 0030 1
- Washington University 1
- Washington University St. Louis 1
- Washington University in St. Louis 1
- Washington University of St. Louis 1
- Washington University School of Medicine in St. Louis 1
- Wahington Univ in St Louis (NT-DMT) 1
- Washington University in St Louis (MRD-HCT) 1
- The John Bouhasin Center for Children with Bleeding Disorders 1
Cincinnati
- Cincinnati Children's Hospital Medical Center 6
- University of Cincinnati 2
- Cincinnati Child's Hsp Med Ctr 1
- Cincinnati Children's Hospital 1
- University of Cincinnati College of Medicine 1
- Cincinnati Children's Hospital Medical Center, Hemophilia & Thrombosis Center 1
- University of Cincinnati Medical Center Hemophilia Treatment Center 1
The Bronx
- Jacobi Medical Center 5
- Montefiore Medical Center 2
- Montefiore Medical Center - Moses Campus- Site Number : 8400057 1
- Montefiore Medical Ctr 1
- Childrens Hospital at Montefiore 1
- Children's Hospital at Montefiore (MRD HCT) 1
- Children's Hospital at Montefiore (NT-DMT) 1
Pittsburgh
- UPMC Children's Hospital of Pittsburgh 3
- University of Pittsburgh 1
- Hillman Cancer Center 1
- Local Institution - 0032 1
- Children's Hospital of Pittsburgh of UPMC 1
- University of Pittsburgh Medical Center (UPMC) 1
- UPMC University of Pittsburgh Classical Hematology Adult Clinic 1
- UPMC Sickle Cell Clinic 1
- University of Pittsburgh Medical Center 1
- Hemophilia Center of Western Pennsylvania 1
Los Angeles
- Children's Hospital Los Angeles - Endocrinology 2
- Children's Hospital Los Angeles 2
- David Geffen School of Medicine at UCLA- Site Number : 8400032 1
- UCLA Health 1
- University of California Los Angeles 1
- University of California, Los Angeles 1
- UCLA Mattel Children's Hospital Ronald Reagan Hospital 1
- Orthopaedic Institute for Children HTC 1
- Childrens Hospital Los Angeles 1
Durham
- Duke University Medical Center 5
- Duke University 2
- Duke Comprehen Sickle Cell 1
- Duke University_Durham 1
- Duke University IDS Pharmacy 1
- Wake Forest Baptist Hospital 1
Columbus
- Nationwide Children's Hospital 2
- The Ohio State University Medical Center 2
- Ohio State Univ Wexner Med Ctr 1
- Ohio State University 1
- The Ohio State University 1
- Ohio State University College of Pharmacy 1
- Nationwide Children's Hospital (NT-DMT) 1
- Ohio State University Medical Center 1
- Nationwide Children's Hospital Columbus 1
Detroit
- Children's Hospital of Michigan 2
- Henry Ford Hospital_Detroit 1
- Detroit Medical Center 1
- Henry Ford Health System 1
- Henry Ford Cancer Center 1
- Henry Ford Health 1
- Functional Fluidics 1
- Central Michigan Children's Hospital of Michigan 1
- Henry Ford Health System Bleeding and Thrombosis Treatment Center 1
Baltimore
- University of Maryland School of Medicine - Baltimore- Site Number : 8400041 1
- The Johns Hopkins University School of Medicine 1
- Johns Hopkins Hospital 1
- University of Maryland 1
- Local Institution - 0064 1
- University of Maryland Medical Center, Stoler Infusion Center 1
- University of Maryland Medical Systems 1
- John Hopkins University School of Medicine 1
- Johns Hopkins University Hemophilia Treatment Center 1
Cleveland
- Univ Hosp Cleveland Med Ctr 1
- Local Institution - 0028 1
- UH Seidman Cancer Center Adult SCD Clinic or UH Rainbow Babies and Children's Hospital Sickle Cell Anemia Center 1
- University Hospitals Clevland Medical Center 1
- The Clevland Clinic Foundation 1
- Cleveland Clinic 1
- University Hospitals Health System Cleveland 1
- University Hospitals Case Medical Center 1
Indianapolis
- Indiana Hemophilia & Thrombosis Center 1
- Indiana University Health Riley Hospital for Children- Site Number : 8400056 1
- Innovative Hematology - Indiana Hemophilia & Thrombosis Center 1
- Riley Children's Hospital (MRD-HCT) 1
- Riley's Children Hospital (NT-DMT) 1
- Indiana University 1
- Indiana Hemophilia and Thrombosis Center 1
Richmond
- Virginia Commonwealth University 3
- Virginia Comm Univ Medical Ctr 2
- VCU Massey Cancer Center: Dalton Oncology Clinic- Site Number : 8400012 1
- Virginia Commonwealth University (VCU) Medical Center 1
Wilmington
- Nemours Children's Health 2
- Nemours/AI duPont Hosp-Chld 1
- Nemours Children's Hospital, Delaware 1
- Nemours Children's Hospital, Delaware (MRD-HCT) 1
- Nemours Children's Hospital 1
- Delaware Hemophilia Treatment Center 1
Oakland
- UCSF Benioff Children's Hospital Oakland 3
- UCSF Oakland Benioff ChildHosp 1
- Univ. of California, San Francisco Health Care 1
- UCSF Benioff Children's Hospital 1
- University of California, San Francisco (UCSF) 1
Charlotte
- Atrium Levine Children's/Atrium Health 1
- Levine Children's Hospital - Hematology 1
- Levine Children's Hospital 1
- Levine Cancer Insitute Carolinas Healthcare System 1
- Atrium Health (MRD-HCT) 1
- St. Jude Affiliate Clinic at Novant Health Hemby Children's Hospital 1
- Novant Health Hemby Children's Hospital 1
Chapel Hill
- Clinical & Translational Research Center (CTRC) 1
- UNC Health 1
- UNC Eastowne Medical Office Building - Consent Only 1
- UNC Children's Hospital (MRD HCT) 1
- UNC Children's Hospital (NT-DMT) 1
- University of North Carolina 1
- Comprehensive Hemophilia Treatment Center, University of North Carolina at Chapel Hill 1
Augusta
- Augusta University 3
- Augusta University Georgia 2
- Center for Blood Disorders Augusta University 1
Phoenix
- Phoenix Children's Hsptl 2
- Phoenix Children's Hospital 2
- Phoenix Children's Hospital- Site Number : 8400028 1
- Arizona Hemophilia and Thrombosis Treatment Center at Phoenix Children's Hospital 1
Orange
- University Of California Irvine 2
- University of California Irvine 2
- Children's Hosp Of Orange 1
- Ctr for Inherited Blood Disorders 1
New Orleans
- Children's Hosp-New Orleans 2
- University Medical Center New Orleans 1
- Manning Family Children's 1
- Children's Hospital of New Orleans 1
- Louisiana Center for Bleeding and Clotting Disorders, Tulane University 1
Rochester
- Mayo Clinic Division of Nursing 1
- University of Rochester Medical Center 1
- University of Rochester (MRD-HCT) 1
- University of Rochester (NT-DMT) 1
- Mayo Comprehensive Hemophilia Center 1
- American Thrombosis and Hemostasis Network 1
Flowood
- Southern Specialty Research 3
- Southern Specialty Clinic 1
- Southern Specialty Research- Site Number : 8400059 1
Miami
- Sylvester Comprehensive Cancer Center- Site Number : 8400020 1
- Univ of Miami/SCCC 1
- Quotient Sciences Sea View 1
- University of Miami Comprehensive Hemophilia Treatment Center 1
- University of Miami Hospital and Clinics 1
Minneapolis
- University of Minnesota 3
- Masonic Cancer Center 1
- Masonic Institute for the Developing Brain 1
Milwaukee
- Medical College of Wisconsin 2
- Versiti, CCBD_Milwaukee 1
- Children's Wisconsin 1
- Comprehensive Center for Bleeding Disorders 1
Nashville
- TriStar Medical Group Children's Specialists - Pediatric Oncology 1
- Vanderbilt University 1
- The Children's Hospital at TriStar Centennial 1
- Tristar Centennial Medical Center 1
- Vanderbilt University Medical Center 1
Hartford
- Connecticut Children's Medical Center 5
New Brunswick
- Site # 8400001 1
- Jack & Sheryl Morris Cancer Center 1
- Robert Wood Johnson University Hospital 1
- Rutgers Cancer Institute of New Jersey 1
Hollywood
- The Foundation for Sickle Cell Disease 2
- Memorial Healthcare 1
- Foundation for Sickle Cell Disease Research 1
Winston-Salem
- Atrium Health-Wake Forest Bapt 2
- Wake Forest University Baptist Medical Center 1
- Wake Forest University Health Sciences 1
Fairfax
- Inova Schar Cancer Institute 2
- Inova Health System 1
- Inova Schar Cancer 1
New Haven
- Smilow Cancer Hospital 1
- Yale-New Haven Hospital 1
- Yale School of Medicine 1
- Yale Hemophilia Treatment Center 1
Baton Rouge
- LSU Health Baton Rouge-North Clinic 1
- Our Lady of the Lake Hospital, Inc. 1
- Our lady of the Lake Hospital 1
- Our Lady of the Lake Regional Medical Center 1
Dallas
- Parkland Memorial Hospital 1
- University of Texas Southwestern Medical Center 1
- North Texas Hemophilia and Thrombosis Program - Pediatric Program / Center for Cancer & Blood Disorders 1
- North Texas Comprehensive Hemophilia Treatment Center 1
Mobile
- Univer South Alabama Ped/Onc 1
- AMR Clinical 1
- University of South Alabama Medical Center 1
Little Rock
- Arkansas Children's Hospital 1
- UAMS Medical Center 1
- Arkansas Center for Bleeding Disorders 1
Newark
- Newark Beth Israel MC 1
- Rutgers New Jersey Medical School 1
- Newark Beth Israel Medical Center - Hemophilia Center 1
Brooklyn
- NYC Health+Hospitals 2
- Interfaith Medical Center 1
Farmington
- University of Connecticut 1
- New England Sickle Cell Institute, University of Connecticut 1
- UConn Health 1
Charleston
- Medical University of South Carolina 2
- Medical University Of South Carolina_Charleston 1
Grand Rapids
- The Cancer and Hematology Centers (CHC) 1
- Helen DeVos Children's Hospital 1
Omaha
- Site # 8400003 1
- Children's Nebraska 1
Ann Arbor
- University of Michigan Health System - Ann Arbor- Site Number : 8400035 1
- The Regents of the University of Michigan 1
Palo Alto
- Stanford University_Palo Alto 1
- Lucile Packard Children's Hospital 1
Torrance
- Harbor-UCLA Medical Center 1
- Harbor UCLA Medical Center 1
Aurora
- Clinical and Transl Res Center 1
- Children's Hospital of Colorado 1
Las Vegas
- Cure 4 the Kids Foundation 1
- Cure 4 The Kids Foundation 1
Queens
- Cohen Children's Medical Ctr 1
- Cohen's Children Hospital (NT-DMT) 1
Oklahoma City
- Univ of OK Health Sciences Ctr 1
- Oklahoma Children's Hospital (MRD-HCT) 1
Norfolk
- Children's Hsptl Of The Kings 1
- Children's Hospital of Kings Daughters 1
Tacoma
- Mary Bridge Children's Health 2
Jacksonville
- University of Florida 1
- Mayo Clinic Florida 1
Riverdale
- WCG Sonar Clinical Research 1
- Sonar Clinical Research 1
Louisville
- Norton Children s Hospital 1
- University of Louisville Hospital 1
West Palm Beach
- Pediatric Hematology / Oncology a division of Kidz Medical services 1
- St. Mary's Medical Center 1
Kansas City
- University Health 1
- Children's Mercy Hospital - Kansas City 1
Sacramento
- UC Davis Comprehensive Cancer Center 1
- University of California at Davis Hemophilia Treatment Center 1
Valhalla
- New York Medical College 2
Gainesville
- University of Florida 1
- University of Florida Hemophilia Treatment Center 1
Providence
- Lifespan 1
- Rhode Island Hospital Hemostasis and Thrombosis Center 1
San Francisco
- University of California San Francisco (UCSF) Medical Center 1
- University of California, San Francisco Hemophilia & Thrombosis Center 1
Irvine
- University of California, Irvine 2
Hackensack
- Hackensack University Medical Center 1
- Hackensack University Hospital (MRD-HCT) 1
Buffalo
- Roswell Park (MRD-HCT) 1
- Western New York BloodCare 1
San Antonio
- UT San Antonio (NT-DMT) 1
- South Texas Comprehensive Hemophilia and Thrombophilia Treatment Center 1
San Diego
- Hemophilia & Thrombosis Treatment Center at UC San Diego Health 1
- Rady Children's Hospital San Diego 1
Tampa
- St. Joseph's Hospital Center for Bleeding & Clotting Disorders 1
- University of South Florida - Adult 1
Peoria
- Bleeding and Clotting Disorders Institute 1
- Children's Hospital of Illinois at OSF-Saint Francis Medical Center 1
Fort Worth
- Cook Childrens Medical Center 1
Jackson
- University of Mississippi Medical Center, Pediatric Emergency Department 1
Clovis
- University of California San Francisco- Site Number : 8400040 1
Coral Springs
- Oncology & Hematology Associates of West Broward- Site Number : 8400029 1
Shreveport
- Louisiana State University Health Sciences Center - Shreveport- Site Number : 8400037 1
Staten Island
- Richmond University Medical Center- Site Number : 8400038 1
Portland
- Oregon Health & Science University (OHSU)- Site Number : 8400043 1
Madera
- Valley Children's Hospital 1
Mount Kisco
- Northwell Health 1
North Canton
- Neuro-Behavioral Clinical Research 1
Easton
- Spoknwrdclinicaltrials 1
Brookline
- Boston Children's Hospital 1
Coral Gables
- University of Miami 1
Plantation
- Edward Jenner Research Group LLC. 1
Dunwoody
- Alpha Clinical Research Georgia 1
Southfield
- Great Lakes Research Institute, Flourish Detroit 1
Madison
- Mississippi Center for Advanced Medicine 1
Morrisville
- UNC IDS 1
Clinton
- Prisma Health Laurens County Hospital 1
Greer
- Prisma Health Greer Memorial Hospital 1
Simpsonville
- Prisma Health Hillcrest Hospital 1
Travelers Rest
- Prisma Health North Greenville Hospital 1
Jamaica
- NYC Health + Hospitals/Queens 1
Falls Church
- Inova Health Care Service 1
Fort Myers
- Golisano Children's Hospital 1
Basking Ridge
- Memorial Sloan Kettering at Basking Ridge (Consent only) 1
Middletown
- Memorial Sloan Kettering Monmouth (Consent only) 1
Montvale
- Memorial Sloan Kettering Bergen (Consent only) 1
Commack
- Memorial Sloan Kettering Suffolk - Commack (Consent only) 1
Harrison
- Memorial Sloan Kettering Westchester (Consent only) 1
Rockville Centre
- Memorial Sloan Kettering Nassau (All protocol activities) 1
Davis
- University of California, Davis 1
Manhattan
- Icahn School of Medicine at Mount Sinai 1
La Jolla
- University of California San Diego - La Jolla 1
Lenexa
- Local Institution - 0001 1
Hickory
- American Thrombosis and Hemostasis Network 1
Duarte
- City of Hope 1
San Bernardino
- Loma Linda Hemoglobinopathy and Inherited Bleeding Disorder Program 1
Orlando
- Arnold Palmer Hospital for Children - The Haley Center for Children's Cancer and Blood Disorders 1
St. Petersburg
- Johns Hopkins All Children's Hospital 1
Savannah
- Memorial Health University Medical Center 1
Iowa City
- Iowa Hemophilia and Thrombosis Center 1
Scarborough
- Maine Hemophilia and Thrombosis Center 1
Reno
- Hemostasis and Thrombosis Center of Nevada 1
Albuquerque
- University of New Mexico Ted R. Montoya Hemophilia & Thrombosis Program 1
Hyde Park
- Northwell Health Hemostasis and Thrombosis Center at Long Island Jewish and Cohen Children's Medical Center 1
Akron
- Akron Children's Hospital - Showers Center for Cancer & Blood Disorders 1
Dayton
- Dayton Children's Hemostasis and Thrombosis Center 1
Toledo
- Northwest Ohio Hemophilia Treatment Center at the Toledo Hospital 1
Austin
- Children's Blood and Cancer Center of Central Texas 1
Seattle
- Washington Center for Bleeding Disorders 1
Green Bay
- Hemophilia Outreach Center Green Bay 1
The Woodlands
- US Wound Registry 1
🇫🇷France121
Paris
- Ap-Hp-Hopital Robert Debre 2
- Hôpital Necker 2
- Novartis Investigative Site 1
- Hôpital Tenon APHP 1
- Department of General Pediatrics and Sickle Cell Center, Necker-Enfants malades Hospital 1
- Investigational Site Number : 2500001 1
- AP-HP-HOPITAL NECKER_Service d'hématologie 1
- Hôpital Necker-Enfants malades 1
- APHP - Centre de Référence des Syndromes 1
- Department of Biotherapy, Necker-Enfants Malades Hospital 1
- Hôpital Universitaire Necker Enfants Malades 1
- Dermatology unit - Cochin Hospital - APHP 1
- Hôpital Européen Georges Pompidou 1
- Necker-Enfants Malades Hospital, Apheresis Unit 1
- Service de Médecine Intensive Réanimation TENON 1
- Hôpital Cochin, Maternité Port-Royal, service de Gynécologie obstétrique 1
- Hôpital Saint Antoine 1
- Hôpital Pitié Salpêtrière 1
- Hôpital Necker-Enfants Malades 1
- Institut Pasteur 1
- Hôpital Robert Debré 1
- Hôpital Trousseau 1
- GHU Paris Psychiatrie et Neurosciences - Hôpital Sainte-Anne 1
- Assistance Publique - Hôpitaux de Paris Hôpital Necker 1
Créteil
- Ap-Hp-Hopital Henri Mondor 2
- Novartis Investigative Site 1
- Investigational Site Number : 2500002 1
- Centre Hospitalier Intercommunal Créteil 1
- Local Institution - 0061 1
- Henri-Mondor 1
- Henri Mondor Hospital 1
- Centre Hospitalier Intercommunal de Creteil 1
- Hôpital Mondor 1
- CHI Créteil 1
- Hôpital Henri Mondor 1
Lyon
- Hospices Civils de Lyon-Hopital Edouard Herriot 2
- Institut d'Hématologie et d'oncologie pédiatrique - IHOPe 1
- HCL-HOPITAL LYON SUD_Institut d'Hématologie et d'Oncologie Pédiatrique (IHOPe) 1
- Hospices Civils de Lyon 1
- Insitut Hématologique et Oncologique Pédiatrique (IHOPe) 1
- Service de Médecine Interne - Hôpital Edouard Herriot 1
Marseille
- CHU La Timone 1
- Investigational Site Number : 2500005 1
- AP-HM Hôpital de La Timone 1
- Assistance Publique Hôpitaux de Marseille - Hôpital de la Timone 1
- Hôpital Nord, AP-HM 1
Bordeaux
- CHU Bordeaux 1
- CHU de Bordeaux - Hôpital Saint-André 1
- Centre Hospitalier Universitaire de Bordeaux-Hopital Pellegrin 1
- Hôpital Pellegrin - Hôpital des Enfants 1
Nantes
- CHU de Nantes 2
- CHU de Nantes, Hotel-Dieu 1
- CHU Nantes 1
Rouen
- CHU Rouen 1
- Centre Hospitalier Universitaire de Rouen-Hopital Charles Nicolle 1
- CHU de Rouen 1
- CHU de Rouen-Hôpital Charles-Nicolle 1
Toulouse
- Oncopole Toulouse 1
- Investigational Site Number : 2500004 1
- CHU de Toulouse 1
- Oncopole - Toulouse Hospital 1
Le Kremlin-Bicêtre
- Hôpital Bicêtre 3
- Hôpital Kremlin-Bicêtre 1
Saint-Denis
- CH Saint-Denis 1
- Centre Hospitalier de Saint-Denis 1
- CH Saint Denis, Hôpital Delafontaine 1
- Centre Hospitalier Saint-Denis 1
Bobigny
- Ap-Hp-Hopital Avicenne 1
- Hôpital Avicenne 1
- Assistance Publique - Hôpitaux de Paris Hôpital Avicenne 1
Orléans
- CHU Orléans 1
- CHU d'Orléans 1
Tours
- CHRU Tours - Hôpital Bretonneau 1
- CHRU de Tours 1
Grenoble
- Centre Hospitalier Universitaire Grenoble Alpes-Site Nord Michallon 1
- CHU Grenoble Alpes 1
Jossigny
- GHEF- Site de Marne-la-Vallée 1
- GHEF, Site de Marne-la-Vallée 1
Lille
- CHU Lille 1
Poitiers
- CHU Poitiers 1
Toulou
- Institut Universitaire du Cancer de Toulouse 1
Roeun
- Centre Hospitalier Universitaire de Rouen-Hopital Charles Nicolle 1
Strasbourg
- CHU Strasbourg-Hautepierre 1
Le Mans
- CH Le Mans 1
Rennes
- CHU de Rennes 1
Bron
- Hôpital Femme Mère Enfant 1
Le Chesnay
- Hospital Versailles 1
Fort-de-France-La Martinique
- CHU de Fort de France 1
Pontoise
- Centre Hospitalier de Pontoise 1
Reims
- Chu Reims 1
Clichy
- Hôpital Beaujon 1
Argenteuil
- Hôpital Victor Dupouy (CH Argenteuil) 1
Aulnay-sous-Bois
- CHI Robert Ballanger 1
Bondy
- Hôpital Jean Verdier 1
Boulogne-Billancourt
- Hôpital Ambroise Paré 1
Bry-sur-Marne
- Hôpital Saint Camille 1
Cergy-Pontoise
- Hôpital NOVO 1
Clamart
- Hôpital Antoine Béclère 1
Corbeil-Essonnes
- CH Sud Francilien 1
Fontainebleau
- CH du Sud Seine et Marne 1
Gonesse
- CH Gonesse 1
Mantes-la-Jolie
- GHT Yvelines Nord 1
Meaux
- GHEF, Site de Meaux 1
Melun
- GH Sud Ile-de-france 1
Montfermeil
- GHI Le Raincy-Montfermeil 1
Neuilly-sur-Seine
- CH Rives de Seine, Site de Neuilly-sur-Seine 1
Nice
- CHU Lenval 1
Orsay
- Hôpital Paris-Saclay 1
Poissy
- CHI Poissy 1
Rambouillet
- CH Rambouillet 1
Versailles
- Hôpital André Mignot 1
Villeneuve-Saint-Georges
- Hôpital Intercommunal Villeneuve-St-Georges 1
🇬🇧United Kingdom54
London
- Guy's Hospital 3
- Whittington Hospital 2
- Guy's Hospital - Haematology 2
- King's College Hospital - Paediatric Research 2
- Kings College Hospital - Haematology 2
- Imperial College London 2
- King's College Hospital 2
- University College London Hospital 2
- The Royal London Hospital 2
- Investigational Site Number : 8260002 1
- Investigational Site Number : 8260001 1
- Evelina London Children's Hospital - Haemophilia 1
- Guy's & St Thomas' NHS Foundation Trust 1
- King's College Hospital NHS Foundation Trust 1
- Hammersmith Hospital, Imperial College Healthcare NHS Trust 1
- Hammersmith Hospital 1
- Central Middlesex Hospital 1
- St George's University Hopsitals NHS Foundation Trust 1
- Hammersmith Hospital Imperial College Healthcare NHS Trust 1
- University College London Hospitals NHS Trust 1
- Guys and St Thomas NHS Foundation Trust / Evelina Childrens Hospital 1
- King's College Hospital - Alex Mowat Research Hub 1
- Local Institution - 0044 1
- Local Institution - 0047 1
- Evelina London Children's Hospital 1
- Kings College Hospital 1
- North Middlesex University Hospital 1
Manchester
- Manchester Royal Infirmary 2
- Investigational Site Number : 8260005 1
- Manchester Royal Infirmary_1 1
- Royal Manchester Children's Hospital 1
Bristol
- University Hospitals Bristol and Weston NHS Foundation Trust 1
- Bristol Royal Infirmary 1
- Zoe Plummer 1
Liverpool
- Royal Liverpool University Hospital 2
Cambridge
- Addenbrooke's Hospital - Haemophilia and Thrombophilia 1
Sheffield
- Royal Hallamshire Hospital 1
East Sussex
- University Hospitals Sussex NHS Foundation Trust 1
Leeds
- Local Institution - 0005 1
Basildon
- Basildon University Hospital 1
Cardiff
- Noah's Ark Children's Hospital for Wales 1
Oxford
- John Radcliffe Hospital 1
🇧🇷Brazil39
São Paulo
- Novartis Investigative Site 3
- Hospital Samaritano De Sao Paulo- Site Number : 0760005 1
- HC da FMUSP Hospital das Clínicas São Paulo 1
- Hospital Samaritano Higienópolis - Instituto de Conhecimento Ensino e Pesquisa (ICEP) 1
- BP A Beneficência Portuguesa de São Paulo 1
- BP - A Beneficência Portuguesa de São Paulo 1
- Casa de Saude Santa Marcelina 1
- Esho Empresa de Servicos Hospitalares S A 1
- Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo 1
Ribeirão Preto
- Novartis Investigative Site 3
- Fundação Hemocentro de Ribeirão Preto 1
- Hospital Das Clinicas da Faculdade de Medicina de Ribeirão Preto - USP 1
Salvador
- Novartis Investigative Site 2
- Hospital Santa Izabel- Site Number : 0760006 1
- Fundação Bahiana de Infectologia- Site Number : 0760009 1
São José do Rio Preto
- Fundação Faculdade Regional de Medicina de São José do Rio Preto- Site Number : 0760001 1
- Fundacao Faculdade Regional de Medicina de Sao Jose do Rio Preto 1
Recife
- MultiHemo - Grupo Oncoclínicas 1
- Multihemo Servicos Medicos S/A 1
Rio de Janeiro
- Hemorio-Fundarj 1
- Instituto Estadual de Hematologia Arthur Siqueira Cavalcanti - HEMORIO 1
Goiânia
- Universidade Federal de Goias- Site Number : 0760002 1
Distrito de Barão Geraldo - Campinas
- Hemocentro UNICAMP 1
São Luís
- Novartis Investigative Site 1
Campinas
- Novartis Investigative Site 1
Sao Jose Rio Preto
- Novartis Investigative Site 1
São
- CPHosp Medicina, Ensino e Pesquisa Ltda 1
🇹🇷Turkey (Türkiye)36
Adana
- Novartis Investigative Site 2
- Başkent Üniversitesi Adana-Hematoloji 2
- Investigational Site Number : 7920001 1
- Investigational Site Number : 7920002 1
- Acıbadem Adana Hastanesi-Hematoloji 1
- Çukurova Üniversitesi Tıp Fakültesi Balcalı Hastanesi- Hematoloji 1
- Baskent Universitesi Adana 1
- Acibadem Adana Hastanesi 1
- Baskent University School of Medicine 1
Ankara
- Hacettepe University Hematology 2
- Hacettepe Üniversitesi Hastanesi- Hematoloji 2
- Hacettepe University Medical Faculty 1
- Hacettepe Universitesi 1
- Hacettepe University pediatric hematology 1
- Novartis Investigative Site 1
Mersin
- Mersin University Medical Faculty Pediatric Hematology 2
- Mersin Üniversitesi Tip Fakültesi Hastanesi- Çiftlikköy Yerleşkesi- Hematoloji 2
- VM Medical Park Mersin Hastanesi- Hematoloji 2
- Investigational Site Number : 7920003 1
Yenişehir
- Mersin University Medical Faculty 1
- Mersin Universitesi 1
Seyhan
- Özel Acibadem Adana Hastanesi 1
- Acıbadem Adana Hastanesi 1
Hatay
- Novartis Investigative Site 1
Mezitli
- VM Medical Park Mersin Hospital 1
Istanbul
- Istanbul Universitesi 1
Mezitli-Mersin
- Medical Park Mersin Hospital 1
Seyhan/Adana
- Özel Acibadem Adana Hastanesi 1
🇮🇹Italy34
Orbassano
- Azienda Ospedaliera Universitaria San Luigi Gonzaga - S.C.D.O. Microcitemie e malattie rare ematologiche 2
- Novartis Investigative Site 1
- Investigational Site Number : 3800007 1
- Azienda Ospedaliera Universitaria San Luigi Gonzaga 1
Verona
- Investigational Site Number : 3800003 1
- Azienda Ospedaliera Universitaria Integrata Verona Policlinico GB Rossi - Borgo Roma - Centro Ricerche Cliniche Di Verona S.r.l. 1
- AOUI Verona and University of Verona 1
- Local Institution - 0009 1
Padova
- Azienda Ospedale Universita Padova 2
- Novartis Investigative Site 1
Naples
- Investigational Site Number : 3800005 1
- A.O.U. Università Studi della Campania "Luigi Vanvitelli" 1
- AORN Antonio Cardarelli 1
Rome
- Investigational Site Number : 3800001 1
- IRCSS Ospedale Pediatrico Bambino Gesu - Dipartimento di Onco-Ematologia e Terapia Cellulare e Genica 1
- IRCCS Bambino Gesù Children's Hospital 1
Genoa
- Investigational Site Number : 3800008 1
- IRCCS Istituto Giannina Gaslini 1
Milan
- Investigational Site Number : 3800004 1
- Local Institution - 0011 1
Palermo
- Investigational Site Number : 3800002 1
- Azienda Ospedaliera Ospedali Riuniti Villa Sofia - Cervello 1
Monza
- Fondazione IRCCS San Gerardo dei Tintori 2
Florence
- Investigational Site Number : 3800006 1
Brescia
- ASST Civili di Brescia 1
Catania
- ARNAS Garibaldi Catania - Presidio Ospedaliero Garibaldi-Centro 1
Modena
- Azienda Ospedaliero Universitaria Di Modena - UOC Pediatria ad indirizzo Oncoematologico 1
Pavia
- Fondazione IRCCS Policlinico San Matteo 1
Cona
- Azienda Ospedaliero-Universitaria di Ferrara - Arcispedale Sant' Anna 1
Padua
- Local Institution - 0037 1
Turin
- University of Turin 1
🇮🇳India32
Raipur
- All India Institute of Medical Sciences (AIIMS), Raipur 3
- AIIMS Raipur 1
Vadodara
- SSG Hospital, Baroda 1
- HOCC Haemato Oncology Care Centre 1
- Haemato Oncology Care Centre 1
New Delhi
- All India Institute of Medical Sciences_New Dehli 1
- All India Institute of Medical Sciences_Delhi 1
- AIIMS Delhi 1
Surat
- Nirmal Hospital Pvt. Ltd. 1
- Nirmal Hospital Pvt Ltd 1
Nagpur
- Arihant Multispeciality Hospital 1
- Indira Gandhi Government Medical College & Hospital 1
Bhubaneswar
- IMS and SUM Hospital 1
- AIIMS, Bhubaneswar 1
Gujarat
- Nirmal Hospital Pvt. Ltd. 2
Maharashtra
- Suretech Hospital and Research Centre Ltd. 2
Guwahati
- Gauhati Medical College and Hospital 1
Dohad
- Zydus Medical College & Hospital 1
Mysuru
- JSS Hospital, Mysore 1
Kozhikode
- Government Medical College, Kozhikode 1
Udaipur
- RNT Medical College 1
Hyderabad
- NIZAM'S Institute of Medical Sciences 1
Noida
- Post Graduate Institute of Child Health 1
Mumbai
- K.J Somaiya Hospital and Research Centre 1
Bangalore
- Victoria Hospital, Bangalore 1
Nashik
- Chopda Medicare & Research Centre Pvt. Ltd: Magnum Heart Institute 1
Delhi
- All India Institute of Medical Sciences-Delhi 1
🇨🇦Canada31
Toronto
- The Hospital for Sick Children 4
- UHN-Toronto General Hospital 1
- University of Toronto 1
- University Health Network - Toronto General Hospital 1
- University Health Network, Toronto General Hospital 1
- The Hospital for Sick Children (MRD-HCT) 1
Montreal
- CHUM-Hosp de Univ Montreal 1
- Montreal Children's Hospital 1
- CHU Ste-Justine 1
- CHU Sainte-Justine 1
- Centre Hospitalier de l'Université de Montréal (CHUM) 1
- McGill University Health Centre 1
- Universite de Montreal / Ste Justine (MRD HCT) 1
Calgary
- Alberta Children's Hospital 2
- Foothills Med Ctr-Univ Calgary 1
- Alberta Children's Hospital (NT-DMT) 1
- Alberta Children's Hospital (MRD-HCT) 1
Vancouver
- St Pauls Hospital 2
- BC Children's Hospital 1
- Local Institution - 0050 1
- British Columbia Children's Hosptial (MRD HCT) 1
Edmonton
- Stollery Children's Hospital 1
- University of Alberta_Edmonton 1
London
- LHSC - Victoria Hospital 1
Scarborough Village
- Scarborough Health Network Research Institute (SHNRI) 1
Winnipeg
- HSC Winnipeg Children's Hospital/University of Manitoba (MRD-HCT) 1
🇳🇬Nigeria26
Lagos
- Lagos University Teaching Hospital, Lagos 4
- Lagos University Teaching Hospital 1
Kano
- Aminu Kano Teaching Hospital 2
- Murtala Muhammad Specialist Hospital 1
- Aminu Kano Teaching Hospital (AKTH) 1
Abuja
- Centre of Excellence for Sickle Cell Disease Research and Training, University of Abuja (CESRTA) 1
- University of Abuja Teaching Hospital, Gwagwalada, Abuja 1
- University Of Abuja Teaching Hospital 1
- University of Abuja 1
Ibadan
- University College Hospital Paediatric Haematology and Oncology Unit, Ibadan 2
- University College Hospital Ibadan 1
- University College Hospital (UCH) 1
Ituku-Ozalla
- University of Nigeria Teaching Hospital (UNTH) 3
Kaduna
- Barau Dikko Teaching Hospital, Kaduna 1
- Kaduna State University 1
Tarauni
- Aminu Kano Teaching Hospital (AKTH) 2
Ile-Ife
- Obafemi Awolowo University Teaching Hospital Complex 1
Zaria
- Ahmadu Bello University 1
🇪🇸Spain24
Barcelona
- Hospital Vall d'Hebron 2
- Novartis Investigative Site 1
- María del Mar 1
- Vall d'hebron Research Institute - Vall d'Hebron Research Institute - University Hospital Vall d'Hebrón (VHIR/HUVH) 1
- Hospital de la Santa Creu i Sant Pau 1
- Hospital Universitari Vall d'Hebron 1
Madrid
- Hospital Universitario La Paz 2
- Novartis Investigative Site 1
- Investigational Site Number : 7240001 1
- Investigational Site Number : 7240002 1
- Hospital Gregorio Marañón 1
- Hospital Clínico San Carlos 1
Terrassa
- Hospital Universitari Mútua de Terrassa 1
- Consorci Sanitari de Terrassa 1
Seville
- Hospital Universitario Virgen del Rocío 1
Barakaldo
- Hospital Universitario de Cruces 1
Esplugues de Llobregat
- Hospital Sant Joan de Déu 1
Granollers
- Hospital General de Granollers 1
Mataró
- Consorci Sanitari del Maresme - Hospital de Mataró 1
Sabadell
- Parc Taulí Hospital Universitari 1
Lleida
- Hospital Universitari Arnau de Vilanova 1
🇰🇪Kenya24
Kisumu
- Ahero Clinical Trials Unit 3
- Kombewa Clinical Research Centre 2
- KEMRI Kondele Children Hospital, Kisumu 1
- Novartis Investigative Site 1
- KEMRI/CRDR, Siaya, KEMRI Clinical Research Annex 1
Nairobi
- Gertrude's Children's Hospital 3
- Kenya Medical Research Institute - Centre for Respiratory Disease Research 1
- Center for Research In Therapeutic Sciences (CREATES), Strathmore University Medical Centre 1
Siaya
- KEMRI CRDR Siaya Clinical Research Annex, Country Referral Hospital 3
- Novartis Investigative Site 1
Eldoret
- International Cancer Institute (ICI) 1
- Novartis Investigative Site 1
Kericho
- KEMRI-Walter-Reed Kericho 2
Ahero
- Novartis Investigative Site 1
🇬🇷Greece19
Athens
- Hippokration Hospital 2
- Investigational Site Number : 3000001 1
- Investigational Site Number : 3000003 1
- "Laiko" General Hospital of Athens 1
- Childrens' Hospital of Athens "Agia Sofia" 1
- Hippokrateio Hospital of Athens 1
- Laiko General Hospital 1
- National and Kapodistrian University of Athens 1
Pátrai
- Investigational Site Number : 3000002 1
- General University Hospital of Patras 1
Thessaloniki
- "AHEPA" University General Hospital of Thessaloniki 1
- 'Ippokrateio' General Hospital of Thessaloniki 1
Larissa
- General Hospital Of Larissa Koutlibaneio And Triantafylleio - Thalassemia and SCD Unit 1
- General Hospital of Larissa 1
Ioannina
- University General Hospital Of Ioannina 1
🇩🇪Germany18
Heidelberg
- Novartis Investigative Site 1
- University Hospital Heidelberg, Department of Pediatric Hematology, Oncology and Immunology 1
- Universitätsklinikum Heidelberg 1
- Center for Child and Adolescent Medicine, University Medical Center Heidelberg 1
Berlin
- Investigational Site Number : 2760005 1
- Charité - Campus Virchow-Klinikum - Klinik für Pädiatrie mit Schwerpunkt Onkologie und Hämatologie 1
- Charité University medicine, Clinic for Hematology, Oncology 1
Düsseldorf
- University Hospital Dusseldorf - Department of Pediatric Oncology, Hematology and Clinical Immunology 1
- University Hospital Duesseldorf, Clinic for Pediatric Oncology, - Hemtaology and Clinical Immunology 1
Essen
- Investigational Site Number : 2760002 1
Stuttgart
- Investigational Site Number : 2760004 1
Freiburg im Breisgau
- Universitätsklinikum Freiburg - Kinder- und Jugendklinik 1
Aachen
- University Hospital Aachen, Children's Hospital 1
Frankfurt
- University Hospital of Frankfurt, Clinic for Paediatrics and Adolescent Medicine 1
Regensburg
- University Hospital Regensburg, Dept. of Ped. Hematology, Oncology and Stem Cell Transplantation 1
Tübingen
- University Children's Hospital Tübingen 1
Würzburg
- University Children's Hospital Würzburg 1
Hamburg
- Universitätsklinikum Hamburg-Eppendorf 1
🇧🇪Belgium17
Brussels
- Novartis Investigative Site 1
- Investigational Site Number : 0560003 1
- Investigational Site Number : 0560002 1
- CHU Saint-Pierre - UMC Sint-Pieter 1
- CHU - UVC Brugmann 1
- HUB - Hôpital Erasme 1
- CHU Saint-Pierre 1
- UZ Brussel Centre for Reproductive Medicine 1
Leuven
- Investigational Site Number : 0560001 1
- UZ Leuven - Kindergeneeskunde 1
- University Hospitals Leuven 1
Edegem
- UZ Antwerpen - UZA - Haematology 1
- UZ Antwerpen - UZA - Kinderhemato-Oncologie 1
- UZ Antwerpen 1
Liège
- Novartis Investigative Site 1
- Investigational Site Number : 0560004 1
Laken
- Novartis Investigative Site 1
🇨🇴Colombia16
Cali
- Novartis Investigative Site 2
- Fundacion Valle del Lili 1
- Centro de investigaciones clínicas, fudación valle del lili 1
Montería
- Novartis Investigative Site 2
- Clínica IMAT Oncomedica Auna S.A.S. 1
Barranquilla
- Novartis Investigative Site 1
- Clinica de la Costa 1
Valledupar
- Novartis Investigative Site 1
- Sociedad de Oncología y Hematología del Cesar SAS (SOHEC) 1
Medellín
- Hospital Pablo Tobon Uribe 1
- Novartis Investigative Site 1
Antioquia
- Sociedad de Oncología y Hematología del Cesar SAS (SOHEC) 1
🇸🇦Saudi Arabia13
Riyadh
- King Khalid University Hospital 3
- Investigational Site Number : 6820003 1
- King Faisal Specialist Hospital & Research Centre, Riyadh 1
- King Saud University Medical City 1
Al Ahsa
- Al-Moosa Health Group 1
- King Abdulaziz Hospital-Al Ahsa-National Guard 1
Al Qaţīf
- Prince Mohammed bin Fahad Hospital for Blood Disorders 1
Dhahran
- National Guard Hospital Dammam 1
Jizan
- Prince Mohammad Bin Naser Hospital 1
Al Mathar Ash Shamali
- King Faisal Specialist Hospital & Research Centre - Riyadh - Hematology 1
Dammam
- King Fahd Hospital of the University 1
🇺🇬Uganda13
Kampala
- Makerere University College of Health Sciences (MakCHS) 1
- Joint Clinical Research Centre (JCRC) 1
- Novartis Investigative Site 1
- Mulago Hospital Sickle Cell Clinic 1
- College of Health Sciences, Makerere University 1
- Makerere University 1
- Minister of Health 1
- National Coordinator EID Program 1
- Sickle Cell Clinic Department of Pediatrics & Child Health Mulago Hospital 1
Jinja
- Jinja Regional Referral Hospital 1
- Nalufenya Childrens 1
Masaka
- Novartis Investigative Site 1
Tororo
- Novartis Investigative Site 1
🇪🇬Egypt12
Cairo
- Faculty of Medicine Ain Shams Medical Research Institute (MASRI) 1
- Faculty of Medicine Ain Shams Research Institute- Clinical Research Center 1
- Faculty of medicine ain shams university 1
Cairo, Egypt
- Cairo University 1
- Abu El-Reesh El-Mounira Children University Hospital 1
Asyut
- Assiut University Hospitals 1
- Assiut University 1
Alexandria, Egypt
- Alexandria University Hospital 1
Alsharkia, Egypt
- Zagazig University Hospital 1
Dokki
- faculty of physical therapy Cairo university 1
Giza
- El-Tahrir st.- in front of Ben El-Sarayat, Ad Doqi Al Giza, Giza Governate 1
🇱🇧Lebanon9
Tripoli
- Hospital Nini 3
- Novartis Investigative Site 1
Beirut
- Novartis Investigative Site 1
- American University of Beirut Medical center 1
Hamra
- American University of Beirut Medical Centre 2
Hazmiyeh
- Chronic Care Center 1
🇳🇱Netherlands7
Amsterdam
- AmsterdamUMC VUMC 1
- Amsterdam UMC - VUmc 1
- Amsterdam UMC 1
Rotterdam
- Investigational Site Number : 5280002 1
- Erasmus MC 1
The Hague
- HagaZiekenhuis 1
Utrecht
- UMC Utrecht, Van Creveldkliniek 1
🇬🇭Ghana7
Accra
- Ghana Institute of Clinical Genetics, Korle Bu Teaching Hospital (KBTH) 1
- Greater Accra Regional Hospital 1
- Korle Bu Teaching Hospital 1
Kintampo
- Kintampo Health Research Centre (KHRC) 2
Navrongo
- Navrongo Health Research Centre 1
Agogo
- Agogo Presbyterian Hospital, Ghana 1
🇴🇲Oman6
Muscat
- Sultan Qaboos University Hospital 3
- Investigational Site Number : 5120001 1
- The Royal Hospital 1
Khoudh
- Novartis Investigative Site 1
🇬🇵Guadeloupe5
Pointe-à-Pitre
- Chu de La Guadeloupe 3
Les Abymes
- CHU Guadeloupe 1
- CHU de la Guadeloupe 1
🇮🇱Israel5
Afula
- Investigational Site Number : 3760001 1
- Investigational Site Number : 3760002 1
- Emek Medical Centre 1
Haifa
- Investigational Site Number : 3760005 1
- Investigational Site Number : 3760006 1
🇦🇺Australia4
Camperdown
- Royal Prince Alfred Hospital - Department of Haematology 1
Randwick
- Prince of Wales Hospital - Department of Haematology 1
Clayton
- Monash Medical Centre - Haematology Department 1
Murdoch
- Fiona Stanley Hospital - Haemophilia and Haemostasis Centre 1
🇨🇳China4
Beijing
- District One Hospital 1
Nanning
- The First Affiliated Hospital of Guangxi Medical University 1
Shanghai
- Children's Hospital of Fudan University 1
Guangzhou
- Guangzhou women and children's medical center 1
🇨🇾Cyprus4
Larnaca
- Larnaca General Hospital 1
Limassol
- Limassol General Hospital 1
Nicosia
- Archbishop Makarios III Hospital 1
Paphos
- Paphos General Hospital 1
🇩🇴Dominican Republic3
Santo Domingo
- Site # 2140001 1
- Site # 2140003 1
- Centro de Obstetricia y Ginecologia 1
🇲🇾Malaysia3
Ampang
- Ampang Hospital 1
Bangi
- Universiti Kebangsaan Malaysia 1
Kota Bharu
- Universiti Sains Malaysia 1
🇨🇮Côte d’Ivoire2
Abidjan
- Yopougon Millionnaire extension health center 1
Yopougon
- Yopougon SCD Center of Excellence 1
🇦🇴Angola2
Luanda
- Hospital Geral dos Cajueiros 1
- Lucrecia Paím Maternity 1
🇮🇪Ireland2
Dublin
- St. James's Hospital 1
- Trinity College Dublin 1
🇹🇿Tanzania2
Mwanza
- Bugando Medical Centre 1
- Buganda Medical Centre 1
🇬🇫French Guiana1
Cayenne
- Centre hospitalier de Cayenne 1
🇦🇹Austria1
Vienna
- St. Anna Kinderspital 1
🇮🇶Iraq1
Baghdad
- Pediatric Hematology Center - Ibn Al-Baladi Maternity & Children Hospital and Hereditary Blood Diseases Center, Al-Karamah Teaching Hospital, Baghdad government. 1
🇯🇲Jamaica1
Kingston
- Caribbean Institute for Health Research, University of West Indies 1
🇦🇷Argentina1
Buenos Aires
- University of Buenos Aires 1
🇧🇳Brunei1
Brunei
- Universiti Brunei Darussalam 1
🇨🇩Democratic Republic of the Congo1
Kinshasa
- Centre Hospitalier Monkole 1
🇩🇰Denmark1
Copenhagen
- Rigshospitalet 1
🇵🇰Pakistan1
Lahore
- University of Lahore 1
🇵🇹Portugal1
Coimbra
- Centro Hospitalar e Universitário de Coimbra 1
🇿🇲Zambia1
Lusaka
- Matero First Level Hospital 1
🇯🇴Jordan1
Amman
- Biosenses 1
Source: ClinicalTrials.gov study locations, fetched 2026-11-10. Counts are trials at that site.